The US Pompe Disease Market Research, Survey and Forecast 2015-2019
The pompe disease market in the US to grow at a CAGR of 10.68 % over the period 2014-2019. Pompe disease, a type of LSD, is caused by mutations in the GAA gene. These mutations inhibit the mechanism of action of GAA, an enzyme responsible for catabolizing glycogen, resulting in accumulation of glycogen in the lysosomes of the cells. The buildup of glycogen in certain organs and tissues, especially in the muscles, hinders the normal functions of the organs. Pompe...
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